Priority 19 (Joint) from the Liver Glycogen Storage Disease (International) PSP
|UNCERTAINTY: When should liver transplantation be considered in patients with liver Glycogen Storage Disease and what are the (dis)advantages and long-term outcomes? (JLA PSP Priority 19 (Joint))|
|JLA question ID||0090/19 (Joint)|
Liver transplantation is a modality of treatment that is indicated for specific situations for patients with liver GSD. However, not much follow-up information on long-term outcomes are known.
For details of the evidence checked, please see the spreadsheet held on the JLA website.
|Health Research Classification System category||Metabolic and endocrine|
|Extra information provided by this PSP|
|Original uncertainty examples||When to consider liver or transplantation for best outcomes? ~ The role and timing of livertransplant in the treatment of GSDI/GSDIII. ~ When is transplant indicated in the absence of significant fibrosis or a tumor? ~ Particular care of these patients in the pre- and post-liver transplantation|
|Submitted by||Patient, carer and healthcare professionals|
|PSP unique ID||0090|
|PSP name||International Glycogen Storage Disease PSP|
|Total number of uncertainties identified by this PSP||72 (To see a full list of all uncertainties identified, please see the detailed spreadsheet held on the JLA website)|
|Date of priority setting workshop||24 May 2019|